Hereditary Angioedema

Long-term safety and effectiveness of berotralstat for hereditary angioedema: the open-label APeX-S study

440.

Farkas, H., Stobiecki, M., Peter, J., Kinaciyan, T., Maurer, M., Aygören-Pürsün, E., Kiani-Alikhan, S., Wu, A., Reshef, A., Bygum, A., Fain, O., Hagin, D., Huissoon, A., Jeseňák, M., Lindsay, K., Grivcheva Panovska, V., Smith, W., Steiner, U. C., Zubrinich, C., Best, J. M., Cornprobst, M., Dix, D., Dobo, S. M., Iocca, H. A., Murray, S. C., Nagy, E., Nagy, E., and Sheridan, W. P.+: Long-term safety and effectiveness of berotralstat for hereditary angioedema: the open-label APeX-S study. Clin. Transl. Allergy 2021: 11; e12035. IF: 5.66

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Oral once-daily berotralstat for the prevention of hereditary angioedema attacks: a randomized, double-blind, placebo-controlled phase 3 trial

434. Zuraw, B., Lumry, W. R., Johnston, D. T., Aygören-Pürsün, E., Banerji, A., Bernstein, J. A., Christiansen, S. C., Jacobs, J. S., Sitz, K. V., Gower, R. G., Gagnon, R., Wedner, J., Kinaciyan, T., Hakl, R., Hanzliková, J., Anderson, J. T., McNeil, D. L., Fritz, S. B., Yang, W., H., Tachdjian, R., Busse, P. J., Craig, T. J., Li, H., Farkas, H., Best, J., M., Clemons, D., Cornpropst, M., Dobo, S. M., Iocca, H. A., Kargl, D., Nagy, E., Murray, S. C., Collis, P., Sheridan, W. P.+, Maurer, M.*, and Riedl, M. A.*: Oral once-daily berotralstat for the prevention of hereditary angioedema attacks: a randomized, double-blind, placebo-controlled phase 3 trial. J. Allergy Clin. Immunol. 2021: 148; 164-172. IF: 14.29

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